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1 |
Material Type: Article
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ESGCT 2022: The New Normal for the Gene Therapy CommunityHuman gene therapy, 2022-09, Vol.33 (17-18), p.841-841 [Peer Reviewed Journal]Copyright Mary Ann Liebert, Inc. Sep 2022 ;ISSN: 1043-0342 ;EISSN: 1557-7422 ;DOI: 10.1089/hum.2022.29217.editorialFull text available |
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2 |
Material Type: Article
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Suppressing Nonsense for Gene TherapyHuman gene therapy, 2022-06, Vol.33 (11-12), p.577-578 [Peer Reviewed Journal]Copyright Mary Ann Liebert, Inc. Jun 2022 ;ISSN: 1043-0342 ;EISSN: 1557-7422 ;DOI: 10.1089/hum.2022.29208.bjc ;PMID: 35537480Full text available |
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3 |
Material Type: Article
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Correction to: ciRS-7 is a prognostic biomarker and potential gene therapy target for renal cell carcinomaMolecular cancer, 2021-12, Vol.20 (1), p.155-155, Article 155 [Peer Reviewed Journal]COPYRIGHT 2021 BioMed Central Ltd. ;2021. This work is licensed under http://creativecommons.org/licenses/by/4.0/ (the “License”). Notwithstanding the ProQuest Terms and Conditions, you may use this content in accordance with the terms of the License. ;The Author(s) 2021 ;ISSN: 1476-4598 ;EISSN: 1476-4598 ;DOI: 10.1186/s12943-021-01459-8 ;PMID: 34861871Full text available |
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4 |
Material Type: Article
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From the Cultural Revolution to the Gene Therapy Revolution: An Interview with Guangping Gao, PhDHuman gene therapy, 2020-02, Vol.31 (3-4), p.135-139 [Peer Reviewed Journal]Copyright Mary Ann Liebert, Inc. Feb 2020 ;ISSN: 1043-0342 ;EISSN: 1557-7422 ;DOI: 10.1089/hum.2020.29109.intFull text available |
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5 |
Material Type: Article
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Targeted gene correction of α1-antitrypsin deficiency in induced pluripotent stem cellsNature (London), 2011-10, Vol.478 (7369), p.391-394 [Peer Reviewed Journal]2015 INIST-CNRS ;ISSN: 0028-0836 ;EISSN: 1476-4687 ;DOI: 10.1038/nature10424 ;PMID: 21993621 ;CODEN: NATUASFull text available |
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6 |
Material Type: Article
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Reviewer recognitionGene therapy, 2021-04, Vol.28 (3-4), p.206-208 [Peer Reviewed Journal]COPYRIGHT 2021 Nature Publishing Group ;The Author(s), under exclusive licence to Springer Nature Limited 2021. ;ISSN: 0969-7128 ;EISSN: 1476-5462 ;DOI: 10.1038/s41434-021-00253-x ;PMID: 33767412Full text available |
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7 |
Material Type: Article
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Stem-Cell Gene Therapy for the Wiskott–Aldrich SyndromeThe New England journal of medicine, 2010-11, Vol.363 (20), p.1918-1927 [Peer Reviewed Journal]Copyright © 2010 Massachusetts Medical Society. All rights reserved. ;2015 INIST-CNRS ;Copyright © 2010 Massachusetts Medical Society. 2010 ;ISSN: 0028-4793 ;EISSN: 1533-4406 ;DOI: 10.1056/NEJMoa1003548 ;PMID: 21067383 ;CODEN: NEJMAGFull text available |
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8 |
Material Type: Article
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Correction to: Schwannoma gene therapy by adeno-associated virus delivery of the pore-forming protein Gasdermin-DCancer gene therapy, 2020-04, Vol.27 (3-4), p.265-265 [Peer Reviewed Journal]COPYRIGHT 2020 Nature Publishing Group ;COPYRIGHT 2020 Nature Publishing Group ;ISSN: 0929-1903 ;EISSN: 1476-5500 ;DOI: 10.1038/s41417-019-0096-8 ;PMID: 31056550Full text available |
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9 |
Material Type: Article
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UNIVERSAL AAV ENHANCER FOR IMPROVED VIRAL TITERS, QUALITY AND REDUCED PRODUCTION COSTS ACROSS SUSPENSION HEK PLATFORMSCytotherapy (Oxford, England), 2024-06, Vol.26 (6), p.S145-S146 [Peer Reviewed Journal]2024 ;ISSN: 1465-3249 ;EISSN: 1477-2566 ;DOI: 10.1016/j.jcyt.2024.03.285Full text available |
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10 |
Material Type: Article
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Reviewer recognitionGene therapy, 2020-04, Vol.27 (3-4), p.180-181 [Peer Reviewed Journal]COPYRIGHT 2020 Nature Publishing Group ;COPYRIGHT 2020 Nature Publishing Group ;Springer Nature Limited 2020. ;ISSN: 0969-7128 ;EISSN: 1476-5462 ;DOI: 10.1038/s41434-020-0130-3 ;PMID: 32099057Full text available |
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11 |
Material Type: Article
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Prevalence of Serum IgG and Neutralizing Factors Against Adeno-Associated Virus (AAV) Types 1, 2, 5, 6, 8, and 9 in the Healthy Population: Implications for Gene Therapy Using AAV VectorsHuman gene therapy, 2010-06, Vol.21 (6), p.704-712 [Peer Reviewed Journal]2015 INIST-CNRS ;COPYRIGHT 2010 Mary Ann Liebert, Inc. ;ISSN: 1043-0342 ;EISSN: 1557-7422 ;DOI: 10.1089/hum.2009.182 ;PMID: 20095819 ;CODEN: HGTHE3Full text available |
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12 |
Material Type: Article
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Reviewer recognitionCancer gene therapy, 2021-04, Vol.28 (3-4), p.351-353 [Peer Reviewed Journal]COPYRIGHT 2021 Nature Publishing Group ;The Author(s), under exclusive licence to Springer Nature America, Inc. 2021. ;ISSN: 0929-1903 ;EISSN: 1476-5500 ;DOI: 10.1038/s41417-021-00322-8 ;PMID: 33785870Full text available |
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13 |
Material Type: Article
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Bone Marrow Mesenchymal Stem Cells: Historical Overview and ConceptsHuman gene therapy, 2010-09, Vol.21 (9), p.1045-1056 [Peer Reviewed Journal]2015 INIST-CNRS ;COPYRIGHT 2010 Mary Ann Liebert, Inc. ;ISSN: 1043-0342 ;EISSN: 1557-7422 ;DOI: 10.1089/hum.2010.115 ;PMID: 20565251 ;CODEN: HGTHE3Full text available |
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14 |
Material Type: Article
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Progress and prospects: immune responses to viral vectorsGene therapy, 2010-03, Vol.17 (3), p.295-304 [Peer Reviewed Journal]2015 INIST-CNRS ;COPYRIGHT 2010 Nature Publishing Group ;COPYRIGHT 2010 Nature Publishing Group ;Copyright Nature Publishing Group Mar 2010 ;Macmillan Publishers Limited 2010. ;ISSN: 0969-7128 ;EISSN: 1476-5462 ;DOI: 10.1038/gt.2009.148 ;PMID: 19907498Full text available |
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15 |
Material Type: Article
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Treatment of Leber Congenital Amaurosis Due to RPE65 Mutations by Ocular Subretinal Injection of Adeno-Associated Virus Gene Vector : Short-Term Results of a Phase I TrialHuman gene therapy, 2008-10, Vol.19 (10), p.979-990 [Peer Reviewed Journal]2008 INIST-CNRS ;COPYRIGHT 2008 Mary Ann Liebert, Inc. ;Copyright 2008, Mary Ann Liebert, Inc. ;ISSN: 1043-0342 ;EISSN: 1557-7422 ;DOI: 10.1089/hum.2008.107 ;PMID: 18774912 ;CODEN: HGTHE3Full text available |
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16 |
Material Type: Article
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Adeno-Associated Virus Serotype 9 Transduction in the Central Nervous System of Nonhuman PrimatesHuman gene therapy, 2012-04, Vol.23 (4), p.382-389 [Peer Reviewed Journal]2015 INIST-CNRS ;Copyright 2012, Mary Ann Liebert, Inc. 2012 ;ISSN: 1043-0342 ;EISSN: 1557-7422 ;DOI: 10.1089/hum.2011.200 ;PMID: 22201473 ;CODEN: HGTHE3Full text available |
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17 |
Material Type: Article
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S68 Towards a first-in-human trial with a pseudotyped lentivirusThorax, 2021-02, Vol.76 (Suppl 1), p.A42-A42 [Peer Reviewed Journal]Author(s) (or their employer(s)) 2021. No commercial re-use. See rights and permissions. Published by BMJ. ;2021 Author(s) (or their employer(s)) 2021. No commercial re-use. See rights and permissions. Published by BMJ. ;ISSN: 0040-6376 ;EISSN: 1468-3296 ;DOI: 10.1136/thorax-2020-BTSabstracts.73Full text available |
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18 |
Material Type: Article
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Recognition of Glioma Stem Cells by Genetically Modified T Cells Targeting EGFRvIII and Development of Adoptive Cell Therapy for GliomaHuman gene therapy, 2012-10, Vol.23 (10), p.1043-1053 [Peer Reviewed Journal]2015 INIST-CNRS ;Copyright 2012, Mary Ann Liebert, Inc. 2012 ;ISSN: 1043-0342 ;EISSN: 1557-7422 ;DOI: 10.1089/hum.2012.041 ;PMID: 22780919 ;CODEN: HGTHE3Full text available |
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19 |
Material Type: Article
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Targeted Gene Correction of Laminopathy-Associated LMNA Mutations in Patient-Specific iPSCsCell stem cell, 2011-06, Vol.8 (6), p.688-694 [Peer Reviewed Journal]2011 Elsevier Inc. ;2015 INIST-CNRS ;Copyright © 2011 Elsevier Inc. All rights reserved. ;2011 Elsevier Inc. 2011 ;ISSN: 1934-5909 ;EISSN: 1875-9777 ;DOI: 10.1016/j.stem.2011.04.019 ;PMID: 21596650Full text available |
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20 |
Material Type: Article
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Optimizing Promoters for Recombinant Adeno-Associated Virus-Mediated Gene Expression in the Peripheral and Central Nervous System Using Self-Complementary VectorsHuman gene therapy, 2011-09, Vol.22 (9), p.1143-1153 [Peer Reviewed Journal]2015 INIST-CNRS ;COPYRIGHT 2011 Mary Ann Liebert, Inc. ;Copyright 2011, Mary Ann Liebert, Inc. 2011 ;ISSN: 1043-0342 ;EISSN: 1557-7422 ;DOI: 10.1089/hum.2010.245 ;PMID: 21476867 ;CODEN: HGTHE3Full text available |