Defining Outcomes for Clinical Trials of Leber Congenital Amaurosis caused by GUCY2D Mutations
American journal of ophthalmology, 2017-05, Vol.177, p.44-57 [Peer Reviewed Journal]Elsevier Inc. ;2017 Elsevier Inc. ;Copyright © 2017 Elsevier Inc. All rights reserved. ;Copyright Elsevier Limited May 1, 2017 ;ISSN: 0002-9394 ;EISSN: 1879-1891 ;DOI: 10.1016/j.ajo.2017.02.003 ;PMID: 28212877
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