Tezacaftor–Ivacaftor in Residual-Function Heterozygotes with Cystic Fibrosis
The New England journal of medicine, 2017-11, Vol.377 (21), p.2024-2035 [Peer Reviewed Journal]Copyright © 2017 Massachusetts Medical Society. All rights reserved. ;ISSN: 0028-4793 ;EISSN: 1533-4406 ;DOI: 10.1056/NEJMoa1709847 ;PMID: 29099333
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